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GEN – Genetic Engineering and Biotechnology News
GEN Edge
Featured News
Multimedia
News
Insights
Topics
Artificial Intelligence
Bioprocessing
Cancer
Drug Discovery
Genome Editing
Infectious Diseases
OMICs
Translational Medicine
Magazine
Browse Issues
Subscribe
Multimedia
Summits
Webinars
GEN Live
Learning Labs
Podcasts
Resources
eBooks/Perspectives
Tutorials
Peer-Reviewed Journals
GEN Biotechnology
Re:Gen Open
New Products
Conference Calendar
Subscribe
Get GEN Magazine
Get GEN eNewsletters
Home
2024
Spinal muscular atrophy
Cancer
Pancreatic Cancer Drugs Could Reflect Alternative Splicing Signatures
Drug Discovery
Novartis, Voyager Ink Up-to-$1.3B Expansion of Neuro Gene Therapy Collaboration
News
Neuromuscular Junction Model Developed Using Pluripotent Stem Cells
Drug Discovery
Base Editing Strategy for Spinal Muscular Atrophy Rescues Patient Fibroblasts, Reverses Mouse Pathology
Drug Discovery
Going Dutch: VectorY’s $138M Series A to Advance Vectorized Antibody Programs for Neurodegenerative Diseases
Drug Discovery
Antibodies Take Center Stage in Alzheimer’s
Drug Discovery
Making AAVs the Go-To for Making Gene Therapies Go
Genome Editing
ASGCT News: David Liu Hails Rapid Progress in Precision Genome Editing
Cancer
Antisense Oligonucleotides Help Treat Deadly Brain Cancer in Mice
Genome Editing
One-Time Treatment: Base Editing Shows Promise vs. SMA
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