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GEN – Genetic Engineering and Biotechnology News
GEN Edge
Featured News
Multimedia
News
Insights
Topics
Artificial Intelligence
Bioprocessing
Cancer
Drug Discovery
Genome Editing
Infectious Diseases
OMICs
Translational Medicine
Magazine
Browse Issues
Subscribe
Multimedia
Summits
Webinars
GEN Live
Learning Labs
Podcasts
Resources
eBooks/Perspectives
Tutorials
Peer-Reviewed Journals
GEN Biotechnology
Re:Gen Open
New Products
Conference Calendar
Subscribe
Get GEN Magazine
Get GEN eNewsletters
Home
2022
Hemophilia B
GEN Edge
Rising Star: Vega Targets Rare Blood Disorders with Antibodies
Alex Philippidis
-
December 27, 2022
0
Genome Editing
First Gene Therapy Approved for Adults with Hemophilia B
John Sterling
-
November 22, 2022
47
Drug Discovery
Hemophilia B Gene Therapy Shows Promise in Clinical Trial
Anjali A. Sarkar, PhD
-
July 22, 2022
0
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News
AstraZeneca -Calquence
®
Alex Philippidis
-
May 18, 2020
0
Drug Discovery
CRISPR “One Shot” Cell Therapy for Hemophilia Developed
GEN Staff Writer
-
May 2, 2018
0
Insights
Improvements to Gene Therapy Clinical Trial Design Benefit Hemophilia Patients
Karen Weintraub
-
December 7, 2017
0
Genome Editing
Sangamo Genome Editing Trial, Assessing MPS II Candidate, Treats First Patient
GEN Staff Writer
-
November 15, 2017
0
Genome Editing
Chiesi Ends Collaboration with uniQure on Hemophilia B Gene Therapy Candidate
GEN Staff Writer
-
August 1, 2017
0
Industry News
uniQure Axing 50 to 60 Positions in Restructuring
GEN Staff Writer
-
November 15, 2016
0
Genome Editing
Novel Gene Therapy Payment Model Proposed
GEN Staff Writer
-
September 9, 2014
0
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