Broadcast Date:
- Time:
The discovery of CRISPR/Cas9 as a simple and effective tool for targeted modification of cells has opened up new possibilities for gene or cell therapies. Join us to hear about strategies for using CRISPR/Cas9 for curing genetic diseases, e.g. sickle cell disease or HIV, its opportunities and challenges. In addition, we will discuss how CRISPR/Cas9 can impact next-generation disease model systems and drug screening, which might be relevant for combinational therapies.
Who Should Attend
- Researchers working on gene or cell therapies
- Translational research scientists
- Clinical researchers
- Process development scientists and pilot-scale scientists
- Chief scientific officers and chief technical officers
- CMO scientists
You Will Learn About
- Introduction to CRISPR/Cas9
- Application examples with focus on use for sickle cell disease
- Opportunities and challenges for the use of CRISPR/Cas9 in gene/cell therapeutic applications
- Use of CRISPR for next-generation disease model systems
- Non-viral transfer of CRISPR/Cas9 cargos and up-scaling of the transfection process
Panelists
Matt Porteus, M.D., Ph.D.
Associate Professor of Pediatrics,
Stanford University
Gregory Alberts, Ph.D.
Global Subject Matter Expert,
Lonza Bioscience Solutions
